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Tag: gene therapy


MHRA approves first ‘gene-editing’ treatment for sickle-cell disease and thalassemia

It can restore healthy haemoglobin production in patients and free them from painful symptoms   The Medicines and Healthcare Products Regulatory Agency (MHRA) has authorised...

European Medicines Agency backs gene therapy to treat rare bleeding disorder

The European Union's health regulator on Friday said it had recommended granting a conditional marketing authorization for a gene therapy by Australian drugmaker CSL...