MHRA approves first ‘gene-editing’ treatment for sickle-cell disease and thalassemia
It can restore healthy haemoglobin production in patients and free them from painful symptoms
The Medicines and Healthcare Products Regulatory Agency (MHRA) has authorised...
European Medicines Agency backs gene therapy to treat rare bleeding disorder
The European Union's health regulator on Friday said it had recommended granting a conditional marketing authorization for a gene therapy by Australian drugmaker CSL...